Study reveals expanding gene therapy for rare disease that causes blindness
Usher Syndrome Type 2A, which is brought on by mutations in the USH2A gene, can cause retinitis pigmentosa as well as hearing loss from birth and gradual visual loss (RP). The light-sensitive layer of the eye called the retina is impacted by RP, and this causes the retina's cells to break down, which results in blindness. There is currently no cure for USH2A.
